BAKER BROS. ADVISORS LP Q1 2018 Filing

Filed May 15, 2018

Portfolio Value

$11.8B

Holdings

114

Report Date

Q1 2018

Filing Type

13F-HR

All Holdings (114 positions)

#StockSharesValue% PortfolioType
1
INCYIncyte Corporation
34,230,751$2.9T24177.41%
2
SGENEURSeattle Genetics, Inc.
49,575,409$2.6T21993.39%
3
ONCBeiGene, Ltd.
5,829,429$979.3B8300.94%
4
ALXNAlexion Pharmaceuticals, Inc.
8,555,894$953.6B8083.07%
5
BMRNBioMarin Pharmaceutical Inc.
7,583,084$614.8B5210.73%
6
ACADACADIA Pharmaceuticals Inc.
27,228,338$611.8B5185.81%
7
Genomic Health, Inc.
13,789,936$431.5B3657.29%
8
ASNDAscendis Pharma A/S
2,837,352$185.6B1572.84%
9
Aquinox Pharmaceuticals, Inc.
10,934,154$154.0B1304.91%
10
AveXis, Inc.
1,167,157$144.2B1222.56%
11
HRTXHeron Therapeutics, Inc.
5,025,298$138.7B1175.61%
12
DBV Technologies S.A.
5,509,560$127.1B1077.35%
13
Ablynx NV
2,176,802$118.8B1006.66%
14
SG7Sage Therapeutics, Inc.
646,828$104.2B883.07%
15
ARRYEURArray BioPharma Inc.
5,656,196$92.3B782.41%
16
Spark Therapeutics, Inc.
1,384,130$92.2B781.23%
17
NBIXNeurocrine Biosciences, Inc.
944,624$78.3B663.99%
18
MRTXEURMirati Therapeutics, Inc.
2,549,461$78.3B663.40%
19
ARGXargenx SE
961,754$77.4B655.73%
20
MDGLMadrigal Pharmaceuticals, Inc.
615,684$71.9B609.48%
21
Idera Pharmaceuticals, Inc.
38,641,462$71.1B602.65%
22
AMRNAmarin Corporation plc
22,669,509$68.2B578.36%
23
BCRXBioCryst Pharmaceuticals, Inc.
14,012,172$66.8B566.52%
24
ERYP1EURERYTECH Pharma S.A.
3,090,069$64.9B550.02%
25
NVAX 3.75 02/01/23Novavax, Inc.
88,500,000$61.9B524.36%
26
CERSCerus Corporation
10,749,937$58.9B499.32%
27
CBAYUSDCymaBay Therapeutics, Inc.
3,917,700$50.9B431.35%
28
RYTMRhythm Pharmaceuticals, Inc.
2,049,020$40.8B345.61%
29
NVTA1EURInvitae Corporation
8,399,411$39.4B333.90%
30
bluebird bio, Inc.
200,000$34.1B289.46%
31
Abeona Therapeutics Inc.
2,184,364$31.3B265.69%
32
HALOHalozyme Therapeutics, Inc.
1,581,424$31.0B262.59%
33
GBYSangamo Therapeutics, Inc.
1,607,579$30.5B258.89%
34
NKTREURNektar Therapeutics
275,396$29.3B248.04%
35
Bellicum Pharmaceuticals, Inc.
4,151,578$27.2B230.84%
36
Menlo Therapeutics Inc.
700,000$26.3B222.97%
37
XNCRXencor, Inc.
872,072$26.1B221.61%
38
GLPGGalapagos NV
259,894$25.9B219.76%
39
EX9Exelixis, Inc.
1,162,644$25.8B218.28%
40
GW Pharmaceuticals plc
221,800$25.0B211.82%
41
MRUSMerus N.V.
1,160,014$21.5B182.19%
42
Aimmune Therapeutics, Inc.
673,908$21.4B181.81%
43
Endocyte, Inc.
2,277,799$20.7B175.50%
44
NTLAIntellia Therapeutics, Inc.
833,795$17.6B149.05%
45
Progenics Pharmaceuticals, Inc.
2,306,184$17.2B145.82%
46
IM8NInsmed Incorporated
700,000$15.8B133.62%
47
MyoKardia, Inc.
290,264$14.2B120.06%
48
BMRN 0.599 08/01/24BioMarin Pharmaceutical Inc.
15,000,000$14.1B119.50%
49
BioMarin Pharmaceutical Inc.
12,228,000$12.5B106.26%
50
Audentes Therapeutics, Inc.
393,222$11.8B100.15%
51
QUREuniQure N.V.
500,000$11.8B99.59%
52
AERIEURAerie Pharmaceuticals, Inc.
215,655$11.7B99.16%
53
ContraFect Corporation
7,153,076$11.6B98.53%
54
AGLEUSDAeglea BioTherapeutics, Inc.
1,137,872$11.3B95.68%
55
Corsicanto II Designated Activity Company
10,000,000$11.0B93.45%
56
Achillion Pharmaceuticals, Inc.
2,856,637$10.6B89.83%
57
CPRXCatalyst Pharmaceuticals, Inc.
4,381,072$10.5B88.75%
58
VNDAVanda Pharmaceuticals Inc.
600,354$10.1B85.74%
59
ASMBAssembly Biosciences, Inc.
193,787$9.5B80.72%
60
ANABAnaptysBio, Inc.
91,086$9.5B80.35%
61
MGNXMacroGenics, Inc.
363,676$9.2B77.56%
62
GLYCEURGlycoMimetics, Inc.
563,312$9.1B77.50%
63
RIGLUSDRigel Pharmaceuticals, Inc.
2,518,882$8.9B75.58%
64
Foamix Pharmaceuticals Ltd.
1,598,991$8.2B69.53%
65
Aevi Genomic Medicine, Inc.
4,055,142$8.2B69.09%
66
BDQMAlbireo Pharma, Inc.
250,000$8.1B69.02%
67
Syros Pharmaceuticals, Inc.
574,835$7.5B63.24%
68
Aegerion Pharmaceuticals, Inc.
9,517,000$7.3B61.65%
69
XLRNAcceleron Pharma Inc.
163,900$6.4B54.31%
70
GTHXEURG1 Therapeutics, Inc.
169,492$6.3B53.23%
71
ALKSAlkermes plc
100,251$5.8B49.25%
72
IFRXInflaRx N.V.
200,000$5.8B48.89%
73
Spring Bank Pharmaceuticals, Inc.
373,144$5.7B48.64%
74
CCXIEURChemoCentryx, Inc.
414,029$5.6B47.73%
75
Momenta Pharmaceuticals, Inc.
308,500$5.6B47.46%
76
Inotek Pharmaceuticals Corp.
5,000,000$4.8B40.64%
77
Nabriva Therapeutics plc
938,235$4.7B40.00%
78
La Jolla Pharmaceutical Company
154,675$4.6B39.04%
79
SLDBSolid Biosciences Inc.
587,884$4.4B37.37%
80
Stemline Therapeutics, Inc.
287,827$4.4B37.33%
81
NVAXNovavax, Inc.
2,000,000$4.2B35.60%
82
Adamas Pharmaceuticals, Inc.
172,630$4.1B34.97%
83
CRBPEURCorbus Pharmaceuticals Holdings, Inc.
660,714$4.0B34.16%
84
Clementia Pharmaceuticals Inc.
250,000$3.8B32.11%
85
NewLink Genetics Corporation
507,273$3.7B31.17%
86
TREURTrillium Therapeutics Inc.
409,323$2.9B24.98%
87
TTPHEURTetraphase Pharmaceuticals, Inc.
935,000$2.9B24.33%
88
Versartis, Inc.
1,426,310$2.4B19.94%
89
JNCEEURJounce Therapeutics, Inc.
100,000$2.2B18.94%
90
NTRANatera, Inc.
228,676$2.1B17.97%
91
Tonix Pharmaceuticals Holdings Corp.
699,500$2.1B17.78%
92
KRYSKrystal Biotech, Inc.
200,000$2.0B17.10%
93
OVIDOvid Therapeutics Inc.
247,733$1.8B14.84%
94
CLLSCellectis S.A.
50,000$1.6B13.36%
95
Trevena, Inc.
950,000$1.6B13.21%
96
Sunesis Pharmaceuticals, Inc.
556,665$1.5B12.83%
97
DVAXDynavax Technologies Corporation
75,000$1.5B12.62%
98
INFIQInfinity Pharmaceuticals, Inc.
580,400$1.2B10.33%
99
MediWound Ltd.
226,000$1.2B9.96%
100
ADAPYAdaptimmune Therapeutics plc
100,000$1.1B9.52%
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