BAKER BROS. ADVISORS LP Q2 2019 Filing

Filed August 14, 2019

Portfolio Value

$14.7T

Holdings

103

Report Date

Q2 2019

Filing Type

13F-HR

All Holdings (103 positions)

#StockSharesValue% PortfolioType
1
SGENEURSeattle Genetics, Inc.
50,057,277$3.5T23.55%
2
INCYIncyte Corporation
31,976,193$2.7T18.46%
3
ONCBeiGene, Ltd.
11,777,285$1.5T9.92%
4
ALXNAlexion Pharmaceuticals, Inc.
8,258,068$1.1T7.35%
5
ACADACADIA Pharmaceuticals Inc.
39,292,086$1.1T7.14%
6
AMRNAmarin Corporation plc
41,544,288$805.5B5.47%
7
BMRNBioMarin Pharmaceutical Inc.
7,589,294$650.0B4.42%
8
Genomic Health, Inc.
9,260,922$538.7B3.66%
9
ASNDAscendis Pharma A/S
3,390,270$390.4B2.65%
10
MRTXEURMirati Therapeutics, Inc.
2,513,462$258.9B1.76%
11
ARGXargenx SE
1,019,557$144.3B0.98%
12
ARRYEURArray BioPharma Inc.
2,848,567$132.0B0.90%
13
MDGLMadrigal Pharmaceuticals, Inc.
1,169,278$122.6B0.83%
14
NBIXNeurocrine Biosciences, Inc.
1,415,283$119.5B0.81%
15
HRTXHeron Therapeutics, Inc.
6,018,104$111.9B0.76%
16
KODKodiak Sciences, Inc.
9,145,115$107.0B0.73%
17
NVTA1EURInvitae Corporation
3,902,421$91.7B0.62%
18
1T7Tricida, Inc.
1,969,905$77.7B0.53%
19
Spark Therapeutics, Inc.
751,927$77.0B0.52%
20
BCELAtreca, Inc.
3,532,760$66.6B0.45%
21
GW Pharmaceuticals plc
370,845$63.9B0.43%
22
IM8NInsmed Incorporated
2,462,216$63.0B0.43%
23
CERSCerus Corporation
10,749,937$60.4B0.41%
24
RYTMRhythm Pharmaceuticals, Inc.
2,708,200$59.6B0.40%
25
Principia Biopharma Inc.
1,787,807$59.3B0.40%
26
Audentes Therapeutics, Inc.
1,506,438$57.0B0.39%
27
ADPTAdaptive Biotechnologies Corporation
1,165,411$56.3B0.38%
28
BCRXBioCryst Pharmaceuticals, Inc.
14,382,673$54.5B0.37%
29
Ra Pharmaceuticals, Inc.
1,801,695$54.2B0.37%
30
MyoKardia, Inc.
1,016,306$51.0B0.35%
31
DBV Technologies S.A.
5,509,560$45.3B0.31%
32
KRYSKrystal Biotech, Inc.
1,034,674$41.7B0.28%
33
CBAYUSDCymaBay Therapeutics, Inc.
5,707,411$40.9B0.28%
34
NBIX 2.25 05/15/24Neurocrine Biosciences, Inc.
30,770,000$40.5B0.28%
35
QUREuniQure N.V.
517,700$40.5B0.27%
36
KNSAKiniksa Pharmaceuticals, Ltd.
2,799,577$37.9B0.26%
37
Zymeworks Inc.
1,708,472$37.6B0.26%
38
Aquinox Pharmaceuticals, Inc.
10,934,154$25.8B0.18%
39
AXSMAxsome Therapeutics, Inc.
772,286$19.9B0.14%
40
XNCRXencor, Inc.
428,120$17.5B0.12%
41
MRUSMerus N.V.
1,160,014$17.0B0.12%
42
BMRN 0.599 08/01/24BioMarin Pharmaceutical Inc.
15,000,000$15.6B0.11%
43
Acorda Therapeutics, Inc.
2,011,189$15.4B0.10%
44
La Jolla Pharmaceutical Company
1,559,231$14.4B0.10%
45
Aimmune Therapeutics, Inc.
673,908$14.0B0.10%
46
Idera Pharmaceuticals, Inc.
4,605,822$12.3B0.08%
47
PTGXProtagonist Therapeutics, Inc.
995,082$12.1B0.08%
48
TPIVDEURMarker Therapeutics, Inc.
1,500,000$11.9B0.08%
49
AGLEUSDAeglea BioTherapeutics, Inc.
1,713,604$11.7B0.08%
50
ASMBAssembly Biosciences, Inc.
803,246$10.8B0.07%
51
GBYSangamo Therapeutics, Inc.
999,823$10.8B0.07%
52
CPRXCatalyst Pharmaceuticals, Inc.
2,559,461$9.8B0.07%
53
Syros Pharmaceuticals, Inc.
974,835$9.0B0.06%
54
ALKSAlkermes plc
400,000$9.0B0.06%
55
Dermira, Inc.
906,943$8.7B0.06%
56
BDQMAlbireo Pharma, Inc.
250,000$8.1B0.05%
57
APLSApellis Pharmaceuticals, Inc.
313,725$8.0B0.05%
58
MISTMilestone Pharmaceuticals Inc.
266,667$7.2B0.05%
59
ANABAnaptysBio, Inc.
113,086$6.4B0.04%
60
Abeona Therapeutics Inc.
1,288,235$6.2B0.04%
61
HOOKGBPHOOKIPA Pharma Inc.
892,857$6.0B0.04%
62
ORTXUSDOrchard Therapeutics plc
405,702$5.7B0.04%
63
HALOHalozyme Therapeutics, Inc.
299,969$5.2B0.04%
64
bluebird bio, Inc.
40,000$5.1B0.03%
65
Bellicum Pharmaceuticals, Inc.
2,677,818$4.6B0.03%
66
Menlo Therapeutics Inc.
700,000$4.2B0.03%
67
GTHXEURG1 Therapeutics, Inc.
127,236$3.9B0.03%
68
NGMUSDNGM Biopharmaceuticals, Inc.
250,000$3.7B0.02%
69
VKTXViking Therapeutics, Inc.
425,000$3.5B0.02%
70
XLRNAcceleron Pharma Inc.
83,900$3.4B0.02%
71
CRNXCrinetics Pharmaceuticals, Inc.
132,985$3.3B0.02%
72
GLPGGalapagos NV
25,072$3.2B0.02%
73
Achillion Pharmaceuticals, Inc.
1,095,359$2.9B0.02%
74
VSAREURAravive, Inc.
484,947$2.9B0.02%
75
XBITXBiotech Inc.
380,442$2.9B0.02%
76
Harpoon Therapeutics, Inc.
214,285$2.8B0.02%
77
Forty Seven, Inc.
250,000$2.6B0.02%
78
AUTLAutolus Therapeutics plc
156,773$2.5B0.02%
79
YMABUSDY-mAbs Therapeutics, Inc.
102,800$2.4B0.02%
80
Cyclerion Therapeutics, Inc.
202,581$2.3B0.02%
81
Spring Bank Pharmaceuticals, Inc.
613,144$2.3B0.02%
82
NXTCNextCure, Inc.
150,000$2.2B0.02%
83
CTMXCytomX Therapeutics, Inc.
194,377$2.2B0.01%
84
Molecular Templates, Inc.
254,230$2.1B0.01%
85
NTLAIntellia Therapeutics, Inc.
128,538$2.1B0.01%
86
IDYAIDEAYA Biosciences, Inc.
200,000$2.0B0.01%
87
CCXIEURChemoCentryx, Inc.
207,029$1.9B0.01%
88
Constellation Pharmaceuticals, Inc.
133,333$1.6B0.01%
89
GLMDGalmed Pharmaceuticals Ltd.
215,594$1.6B0.01%
90
Aileron Therapeutics, Inc.
2,040,000$1.5B0.01%
91
Dova Pharmaceuticals, Inc.
99,405$1.4B0.01%
92
Foamix Pharmaceuticals Ltd.
498,189$1.2B0.01%
93
Sierra Oncology, Inc.
2,000,000$1.1B0.01%
94
Adamas Pharmaceuticals, Inc.
172,630$1.1B0.01%
95
INFIQInfinity Pharmaceuticals, Inc.
580,400$1.0B0.01%
96
RCUSArcus Biosciences, Inc.
121,534$966.0M0.01%
97
FLGTFulgent Genetics, Inc.
125,000$835.0M0.01%
98
Affimed N.V.
200,000$574.0M0.00%
99
AQSTAquestive Therapeutics, Inc.
99,600$418.0M0.00%
100
Sunesis Pharmaceuticals, Inc.
556,665$405.0M0.00%
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