BAKER BROS. ADVISORS LP Q4 2017 Filing

Filed February 14, 2018

Portfolio Value

$11.5T

Holdings

123

Report Date

Q4 2017

Filing Type

13F-HR

All Holdings (123 positions)

#StockSharesValue% PortfolioType
1
INCYIncyte Corporation
34,230,523$3.2T28.10%
2
SGENEURSeattle Genetics, Inc.
45,725,556$2.4T21.20%
3
ALXNAlexion Pharmaceuticals, Inc.
8,553,864$1.0T8.87%
4
ACADACADIA Pharmaceuticals Inc.
27,228,338$819.8B7.11%
5
BMRNBioMarin Pharmaceutical Inc.
7,583,084$676.2B5.86%
6
Genomic Health, Inc.
13,781,102$471.3B4.09%
7
ONCBeiGene, Ltd.
3,849,231$376.1B3.26%
8
DBV Technologies S.A.
5,509,560$135.5B1.17%
9
Aquinox Pharmaceuticals, Inc.
10,934,154$128.6B1.11%
10
ASNDAscendis Pharma A/S
2,618,818$104.9B0.91%
11
Ablynx NV
4,161,118$104.0B0.90%
12
SG7Sage Therapeutics, Inc.
616,514$101.5B0.88%
13
AMRNAmarin Corporation plc
22,669,509$90.9B0.79%
14
AveXis, Inc.
775,000$85.8B0.74%
15
NBIXNeurocrine Biosciences, Inc.
1,004,624$77.9B0.68%
16
ARRYEURArray BioPharma Inc.
5,656,196$72.4B0.63%
17
Spark Therapeutics, Inc.
1,384,130$71.2B0.62%
18
BCRXBioCryst Pharmaceuticals, Inc.
13,997,172$68.7B0.60%
19
ERYP1EURErytech Pharma S.A.
3,090,069$68.0B0.59%
20
NVTA1EURInvitae Corporation
7,288,300$66.2B0.57%
21
ARGXargenx SE
961,754$60.7B0.53%
22
RYTMRhythm Pharmaceuticals, Inc.
2,049,020$59.5B0.52%
23
MDGLMadrigal Pharmaceuticals, Inc.
615,684$56.5B0.49%
24
HRTXHeron Therapeutics, Inc.
3,060,641$55.4B0.48%
25
MRTXEURMirati Therapeutics, Inc.
2,549,461$46.5B0.40%
26
EX9Exelixis, Inc.
1,506,499$45.8B0.40%
27
Bellicum Pharmaceuticals, Inc.
5,032,313$42.3B0.37%
28
NVAX 3.75 02/01/23Novavax, Inc.
88,500,000$40.9B0.35%
29
Idera Pharmaceuticals, Inc.
18,315,802$38.6B0.33%
30
Ignyta, Inc.
1,384,266$37.0B0.32%
31
bluebird bio, Inc.
200,000$35.6B0.31%
32
GBYSangamo Therapeutics, Inc.
2,113,376$34.7B0.30%
33
CERSCerus Corporation
9,745,209$32.9B0.29%
34
HALOHalozyme Therapeutics, Inc.
1,581,424$32.0B0.28%
35
Abeona Therapeutics Inc.
1,984,364$31.5B0.27%
36
Acorda Therapeutics, Inc.
35,083,000$29.8B0.26%
37
GW Pharmaceuticals plc
221,800$29.3B0.25%
38
CBAYUSDCymaBay Therapeutics, Inc.
2,991,775$27.5B0.24%
39
Aimmune Therapeutics, Inc.
673,908$25.5B0.22%
40
GLPGGalapagos NV
259,894$24.4B0.21%
41
CPRXCatalyst Pharmaceuticals, Inc.
5,852,153$22.9B0.20%
42
MRUSMerus N.V.
1,160,014$22.5B0.20%
43
NTLAIntellia Therapeutics, Inc.
1,145,453$22.0B0.19%
44
IM8NInsmed Incorporated
700,000$21.8B0.19%
45
XNCRXencor, Inc.
872,072$19.1B0.17%
46
Progenics Pharmaceuticals, Inc.
3,150,808$18.7B0.16%
47
ANABAnaptysBio, Inc.
181,386$18.3B0.16%
48
AERIEURAerie Pharmaceuticals, Inc.
299,356$17.9B0.16%
49
IMGNEURImmunoGen, Inc.
2,563,489$16.4B0.14%
50
MyoKardia, Inc.
355,264$15.0B0.13%
51
BMRN 0.599 08/01/24BioMarin Pharmaceutical Inc.
15,000,000$14.9B0.13%
52
Foamix Pharmaceuticals Ltd.
2,466,702$14.8B0.13%
53
ASMBAssembly Biosciences, Inc.
322,727$14.6B0.13%
54
BioMarin Pharmaceutical Inc.
12,228,000$13.2B0.11%
55
NKTREURNektar Therapeutics
171,934$10.3B0.09%
56
LGNDLigand Pharmaceuticals Incorporated
73,386$10.0B0.09%
57
Stemline Therapeutics, Inc.
633,497$9.9B0.09%
58
RIGLUSDRigel Pharmaceuticals, Inc.
2,518,882$9.8B0.08%
59
GLYCEURGlycoMimetics, Inc.
563,312$9.5B0.08%
60
QUREuniQure N.V.
482,557$9.5B0.08%
61
ITCIEURIntra-Cellular Therapies, Inc.
609,166$8.8B0.08%
62
Achillion Pharmaceuticals, Inc.
2,856,637$8.2B0.07%
63
ALKSAlkermes plc
150,251$8.2B0.07%
64
NewLink Genetics Corporation
1,007,273$8.2B0.07%
65
Aegerion Pharmaceuticals, Inc.
9,517,000$7.6B0.07%
66
AGIOAgios Pharmaceuticals, Inc.
128,666$7.4B0.06%
67
ContraFect Corporation
7,153,076$7.2B0.06%
68
XLRNAcceleron Pharma Inc.
163,900$7.0B0.06%
69
MGNXMacroGenics, Inc.
363,676$6.9B0.06%
70
VNDAVanda Pharmaceuticals Inc.
423,884$6.4B0.06%
71
AGLEUSDAeglea BioTherapeutics, Inc.
1,137,872$6.2B0.05%
72
TTPHEURTetraphase Pharmaceuticals, Inc.
935,000$5.9B0.05%
73
Adamas Pharmaceuticals, Inc.
172,630$5.8B0.05%
74
Nabriva Therapeutics plc
938,235$5.6B0.05%
75
Syros Pharmaceuticals, Inc.
574,835$5.6B0.05%
76
BDQMAlbireo Pharma, Inc.
200,000$5.1B0.04%
77
Spring Bank Pharmaceuticals, Inc.
373,144$5.0B0.04%
78
La Jolla Pharmaceutical Company
154,675$5.0B0.04%
79
Aevi Genomic Medicine, Inc.
4,055,142$4.9B0.04%
80
Clementia Pharmaceuticals Inc.
250,000$4.7B0.04%
81
CRBPEURCorbus Pharmaceuticals Holdings, Inc.
660,714$4.7B0.04%
82
Endocyte, Inc.
1,087,323$4.7B0.04%
83
Advanced Accelerator Applications S.A.
55,125$4.5B0.04%
84
Acorda Therapeutics, Inc.
205,966$4.4B0.04%
85
IFRXInflaRx N.V.
200,000$4.2B0.04%
86
INOTEK Technologies Corp.
5,000,000$4.0B0.03%
87
OVIDOvid Therapeutics Inc.
333,333$3.3B0.03%
88
Versartis, Inc.
1,426,310$3.1B0.03%
89
Akari Therapeutics Plc
696,901$3.0B0.03%
90
TREURTrillium Therapeutics Inc.
409,323$3.0B0.03%
91
Epizyme, Inc.
232,481$2.9B0.03%
92
SELBUSDSelecta Biosciences, Inc.
283,716$2.8B0.02%
93
Sunesis Pharmaceuticals, Inc.
741,665$2.7B0.02%
94
Protalix BioTherapeutics, Inc.
3,423,000$2.6B0.02%
95
NVAXNovavax, Inc.
2,000,000$2.5B0.02%
96
Tonix Pharmaceuticals Holdings Corp.
699,500$2.4B0.02%
97
KRYSKrystal Biotech, Inc.
200,000$2.1B0.02%
98
KPTIEURKaryopharm Therapeutics Inc.
216,990$2.1B0.02%
99
NTRANatera, Inc.
228,676$2.1B0.02%
100
Trevena, Inc.
950,000$1.5B0.01%
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